We would be very grateful for your help with a short questionnaire about your experiences with sapropterin so far. The survey is open to anyone in the UK: adults with PKU, parents, and carers. The questionnaire asks about: • Whether you or your child have been offered sapropterin • If so, how the response test went • If you were not a responder or have not been offered sapropterin, we would like to hear about your experience • If you are a responder, how things are going for you on sapropterin
You can complete the questionnaire here: Patient-Reported Experiences of Sapropterin in PKU in the UK
